Genetic therapies for cystic fibrosis can be inhaled or given through an IV. However, getting these therapies into the correct cells in the lungs is not easy, and each of these delivery methods involves specific challenges.
This animation, originally featured in “Working Together to Pave the Path to a Cure,” at NACFC 2021, discusses the challenges of tissue or cell-specific delivery of gene therapy for people with cystic fibrosis.
Originally recorded September 17, 2021. Featured in plenary 2 of NACFC 2021.